
CDER’s Progress in Rare Diseases
Orphanet Journal of Rare Diseases is proud to present this piece, authored by the Rare Diseases Team within the U.S. Food & Drug… Read more »
Orphanet Journal of Rare Diseases is proud to present this piece, authored by the Rare Diseases Team within the U.S. Food & Drug… Read more »
In this blog, Dr. Anne R. Pariser (Director of the Office of Rare Diseases Research, at the NIH's National Center for Advancing Translational… Read more »
Orphanet Journal of Rare Diseases is proud to present this piece, a runner-up entry in Findacure and Medics4RareDiseases' "Student… Read more »
Patients with LAM (lymphangioleiomyomatosis) or other rare lung diseases can lose their exercise capacity because of dyspnea and… Read more »
Orphanet Journal of Rare Diseases is proud to present this piece, a runner-up entry in Findacure and Medics4RareDiseases' "Student… Read more »
Orphanet Journal of Rare Diseases is proud to present this piece, a runner-up entry in Findacure and Medics4RareDiseases' "Student… Read more »
In a blog for Ovarian Cancer Awareness Month, Christina Uwins and Simon Butler-Manuel discuss the MIRRORS study registered at the… Read more »
In a blog for World Cancer Day, Dr Vinton Cheng and Dr Amy Kwan discuss the PRIMROSE audit registered at the ISRCTN registry.
In a blog for World Cancer Day, Dr Hayley Wright discusses the digital HOPE programme for people living with cancer during… Read more »
For World AIDS Day 2020, this blog takes a look at studies registered at the ISRCTN registry during the previous 12 months.